Author Archives: Alice Melão

Potential Gene Therapy May Improve Survival in MNGIE Patients, Mouse Study Suggests

A gene therapy designed to correct the underlying defect that causes mitochondrial neurogastrointestinal encephalomyopathy (MNGIE) could potentially improve survival in patients with the disease, a mouse study suggests. The potential therapeutic strategy was described in the study, “Long-Term Sustained Effect of Liver-Targeted Adeno-Associated Virus Gene Therapy for Mitochondrial…

Patent Likely to Be Issued to Mitochon for Mitochondria-targeted Therapies

The U.S. Patent and Trade Mark Office (USPTO) sent a notice of allowance — meaning it intends to issue a patent — to Mitochon Pharmaceuticals regarding the clinical development of its investigative drug MP101 for the treatment of several mitochondrial-related diseases, including Huntington’s disease and Duchenne muscular dystrophy, among others.