• NORD Partners with ‘Sing Me a Story’ for July 18–20 Living Rare Forum
  • Global Rare Disease Group’s Focus: 1,000 New Therapies by 2027, Despite COVID-19
  • 2 New Mutations in Mitochondrial Genes Linked to Complex I Deficiency
  • Pediatric Rare Disease Therapies Increase, But Most Repurposed, Study Finds
  • New Mitochondrial Gene Mutation Speeds GRACILE Progression, Study Shows
  • Video: BioNews’ Social Media Campaign Highlights #WhatMakesMeRare
  • Elsevier Opens Books, Review Articles to Rare Disease Researchers Starting Feb. 29
  • Advice on Starting Nonprofit Groups for Rare and Other Diseases Focus of NORD Webinar
  • Patients, Supporters Worldwide Recognizing Rare Disease Day 2020
  • Elamipretide Improves Physical Fitness Compared to Natural Disease Course in Barth Syndrome, Analysis Shows
  • Gene Discovery in Fruit Fly Study May Help Uncover Treatments for Mitochondrial Disease in People
  • FDA Efforts to Bring Patients into Treatment Decisions Focus of NORD Webinar