• Clinicians Should Consider Different Wording in Cases of Unconfirmed Mitochondrial Disease, Study Suggests
  • MDA Conference Bringing Neuromuscular Disease Experts to Orlando to Share ‘New Era’ in Treatment, Research
  • New Phase 1 Trial of Potential Treatment for Mitochondrial Diseases, KL1333, Enrolling in UK
  • University of Arkansas Team Awarded NIH Grant to Find Better Diagnostic Tools for Mitochondrial Diseases
  • Brexit Could Have Real Effects for UK Rare Disease Patients, Experts Warn
  • Moral Dilemmas Complicate Treatment of Rare Diseases, Says Israeli Bioethicist
  • NIH Rare Disease Day Highlights Joint Networks Advancing Array of Research
  • WODC 2019 Organizers Expect 1,200 to Attend Rare Disease Conference in April
  • Vienna to Host RARE2019 Meeting on Rare Diseases
  • Patients, Family and Friends to Take Part in Variety of Rare Disease Day Events Worldwide
  • Topline Results Announced for Phase 3 Trial Testing GS010 in LHON Patients
  • FDA Revising ‘Draft Guidance’ on Developing Treatments for Rare Diseases