• Symptoms Vary Greatly in People with MT-ATP6 Mutations and Better Tests Needed, Study Says
  • Kidney Disorder Therapy May Be Effective in Mitochondrial Disease, Study Suggests
  • Reneo Pharmaceuticals Raises $50M to Support Development of Therapies for Mitochondrial Diseases
  • Top-line Results Expected This Year for Phase 3 Study Testing Elamipretide Injections for Mitochondrial Myopathy
  • Rare Diseases Constitute a ‘Public Health Issue,’ NCATS Director Warns
  • GS010 Gene Therapy Continues to Improve Vision Clarity in LHON Patients, New Phase 3 Data Show
  • Clinicians Should Consider Different Wording in Cases of Unconfirmed Mitochondrial Disease, Study Suggests
  • MDA Conference Bringing Neuromuscular Disease Experts to Orlando to Share ‘New Era’ in Treatment, Research
  • New Phase 1 Trial of Potential Treatment for Mitochondrial Diseases, KL1333, Enrolling in UK
  • University of Arkansas Team Awarded NIH Grant to Find Better Diagnostic Tools for Mitochondrial Diseases
  • Brexit Could Have Real Effects for UK Rare Disease Patients, Experts Warn
  • Moral Dilemmas Complicate Treatment of Rare Diseases, Says Israeli Bioethicist